marketcaparena

NGNE

Neurogene Inc.

Company overview

Market capitalization
$569.92M
Employees
131
Latest publication
2026-09-29
About Neurogene Inc.

Neurogene Inc., a clinical stage biotechnology company, develops genetic medicines for rare neurological diseases. The company's product candidates include NGN-401 that is packaged in an adeno-associated virus 9, which is in Phase 1/2 clinical trial for the treatment of Rett syndrome; and NGN-101, a conventional gene therapy candidate that is in Phase 1/2 clinical trial to treat CLN5 Batten disease. It has a license agreement with The University of Edinburgh, Virovek, Inc., Sigma-Aldrich Co. LLC., and Leland Stanford Junior University. The company was founded in 2018 and is headquartered in New York, New York.

Company website

Financial statements

Income Quarterly

Exact reported values; units shown beside each amount. Missing values are —.
MetricQ1 20262026-03-31 · USDQ4 20252025-12-31 · USDQ3 20252025-09-30 · USDQ2 20252025-06-30 · USDQ1 20252025-03-31 · USDQ4 20242024-12-31 · USDQ3 20242024-09-30 · USDQ2 20242024-06-30 · USD
Total Revenue0USD0USD0USD0USD0USD-925,000USD0USD925,000USD
Cost Of Revenue854,000USD787,000USD—812,000USD762,000USD15,347,000USD812,000USD817,000USD
Gross Profit-854,000USD-787,000USD—-812,000USD-762,000USD-15,347,000USD-812,000USD108,000USD
Research Development25,150,000USD20,639,000USD17,241,000USD19,366,000USD17,760,000USD15,347,000USD16,285,000USD15,744,000USD
Selling General Administrative8,199,000USD6,890,000USD6,557,000USD6,715,000USD8,159,000USD6,165,000USD5,895,000USD5,315,000USD
Total Operating Expenses32,495,000USD26,742,000USD23,798,000USD26,081,000USD25,919,000USD6,165,000USD22,180,000USD20,242,000USD
Operating Income-33,349,000USD-27,529,000USD-23,798,000USD-26,081,000USD-25,919,000USD-21,512,000USD-22,180,000USD-20,134,000USD
Interest Income2,261,000USD2,673,000USD2,739,000USD2,928,000USD3,206,000USD2,270,000USD1,842,000USD2,035,000USD
Interest Expense0USD1,000USD1,000USD1,000USD2,000USD2,000USD3,000USD4,000USD
Net Interest Income2,261,000USD2,672,000USD2,738,000USD2,927,000USD3,204,000USD2,268,000USD1,839,000USD2,031,000USD
Income Before Tax-30,934,000USD-24,735,000USD-20,953,000USD-22,016,000USD-22,647,000USD-19,514,000USD-20,217,000USD-18,492,000USD
Net Income-30,934,000USD-24,735,000USD-20,953,000USD-22,016,000USD-22,647,000USD-19,514,000USD-20,217,000USD-18,492,000USD
Net Income From Continuing Ops-30,934,000USD-24,735,000USD-20,953,000USD-22,016,000USD-22,647,000USD-19,514,000USD-20,217,000USD-18,492,000USD
Ebit-33,349,000USD-27,529,000USD-20,952,000USD-22,015,000USD-22,645,000USD-21,512,000USD-20,214,000USD-18,488,000USD
Ebitda-32,495,000USD-26,742,000USD-20,176,000USD-21,248,000USD-21,883,000USD-20,714,000USD-19,407,000USD-17,671,000USD
Depreciation And Amortization854,000USD787,000USD776,000USD767,000USD762,000USD798,000USD807,000USD817,000USD
Reconciled Depreciation854,000USD787,000USD776,000USD767,000USD762,000USD798,000USD807,000USD817,000USD
Total Other Income Expense Net2,415,000USD2,794,000USD2,845,000USD4,065,000USD3,272,000USD1,998,000USD1,963,000USD1,642,000USD
Unclassified Operating Expenses—————-15,347,000USD——
Income Tax Expense———————-1USD
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Income Yearly

Exact reported values; units shown beside each amount. Missing values are —.
MetricFY 20252025-12-31 · USDFY 20242024-12-31 · USDFY 20232023-12-31 · USDFY 20222022-12-31 · USDFY 20212021-12-31 · USDFY 20202020-12-31 · USDFY 20192019-12-31 · USDFY 20182018-12-31 · USD
Total Revenue0USD925,000USD0USD0USD0USD——25,000,000USD
Cost Of Revenue3,192,000USD3,247,000USD3,262,000USD3,196,000USD42,264,000USD1,821,000USD340,000USD—
Gross Profit-3,192,000USD-2,322,000USD-3,262,000USD-3,196,000USD-42,264,000USD-1,821,000USD-340,000USD25,000,000USD
Research Development75,011,000USD60,917,000USD44,394,000USD47,505,000USD42,264,000USD24,344,000USD6,317,000USD32,789,000USD
Selling General Administrative28,317,000USD22,613,000USD11,189,000USD9,012,000USD8,270,000USD———
Unclassified Operating Expenses-3,312,000USD-3,247,000USD-3,262,000USD-3,196,000USD-42,264,000USD15,389,000USD17,786,000USD15,735,000USD
Total Operating Expenses100,016,000USD80,283,000USD52,321,000USD53,321,000USD8,270,000USD39,733,000USD24,103,000USD48,524,000USD
Operating Income-103,208,000USD-82,605,000USD-55,583,000USD-56,517,000USD-50,534,000USD-41,554,000USD-24,443,000USD-23,524,000USD
Interest Income11,547,000USD8,467,000USD2,951,000USD1,337,000USD17,000USD———
Interest Expense5,000USD12,000USD12,000USD2,000USD0USD—1,000USD4,000USD
Net Interest Income11,542,000USD8,455,000USD2,939,000USD1,335,000USD17,000USD———
Income Before Tax-90,351,000USD-75,144,000USD-36,317,000USD-55,189,000USD-50,517,000USD-33,277,000USD-69,442,000USD-31,585,000USD
Net Income-90,351,000USD-75,144,000USD-36,317,000USD-55,189,000USD-50,517,000USD-33,277,000USD-69,442,000USD-31,585,000USD
Net Income From Continuing Ops-90,351,000USD-75,144,000USD-36,317,000USD-55,189,000USD-50,517,000USD———
Ebitda-103,328,000USD-71,885,000USD-52,286,000USD-51,991,000USD-49,587,000USD-31,456,000USD-69,101,000USD-31,581,000USD
Reconciled Depreciation3,092,000USD3,247,000USD3,297,000USD3,200,000USD947,000USD———
Total Other Income Expense Net12,857,000USD7,461,000USD19,266,000USD1,328,000USD17,000USD8,277,000USD-44,999,000USD-8,061,000USD
Ebit—-75,132,000USD-55,583,000USD-55,187,000USD-50,534,000USD-33,277,000USD-69,441,000USD—
Depreciation And Amortization—3,247,000USD3,297,000USD3,196,000USD947,000USD1,821,000USD340,000USD—
Income Tax Expense——-16,000USD-5,000USD17,000USD-1USD168,140USD—
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Balance sheet Quarterly

Exact reported values; units shown beside each amount. Missing values are —.
MetricQ2 20262026-06-30 · USDQ1 20262026-03-31 · USDQ4 20252025-12-31 · USDQ3 20252025-09-30 · USDQ2 20252025-06-30 · USDQ1 20252025-03-31 · USDQ4 20242024-12-31 · USDQ3 20242024-09-30 · USD
Total Assets244,364,000USD263,141,000USD289,176,000USD287,832,000USD297,316,000USD315,301,000USD335,730,000USD164,120,000USD
Cash And Equivalents112,485,000USD———————
Cash And Short Term Investments225,392,000USD243,182,000USD269,013,000USD265,410,000USD274,519,000USD292,602,000USD312,405,000USD138,993,000USD
Short Term Investments112,907,000USD119,021,000USD165,168,000USD194,405,000USD215,706,000USD221,831,000USD175,819,000USD72,360,000USD
Total Current Assets228,913,000USD246,747,000USD271,579,000USD270,519,000USD278,986,000USD296,398,000USD315,923,000USD143,647,000USD
Other Current Assets132,000USD3,565,000USD2,106,000USD4,249,000USD3,158,000USD3,200,000USD2,870,000USD3,982,000USD
Other Non Current Assets1,107,000USD———————
Total Liabilities27,231,000USD———————
Total Current Liabilities21,505,000USD18,866,000USD16,411,000USD14,710,000USD15,440,000USD14,094,000USD15,157,000USD15,800,000USD
Other Current Liabilities1,078,000USD———————
Other Non Current Liabilities0USD———————
Total Stockholder Equity217,133,000USD237,783,000USD264,887,000USD265,540,000USD273,255,000USD291,795,000USD310,375,000USD137,414,000USD
Total Equity Including Noncontrolling Interest217,133,000USD———————
Property Plant Equipment Net13,997,000USD14,977,000USD15,462,000USD15,911,000USD16,895,000USD17,668,000USD18,493,000USD19,345,000USD
Accounts Payable3,294,000USD4,685,000USD1,953,000USD1,544,000USD2,060,000USD3,063,000USD1,336,000USD1,684,000USD
Short Term Debt3,021,000USD3,047,000USD3,064,000USD3,742,000USD4,283,000USD4,182,000USD2,999,000USD3,678,000USD
Common Stock0USD———————
Retained Earnings-418,071,000USD-383,583,000USD-352,649,000USD-327,914,000USD-306,961,000USD-284,945,000USD-262,298,000USD-242,784,000USD
Total Liab—25,358,000USD24,289,000USD22,292,000USD24,061,000USD23,506,000USD25,355,000USD26,706,000USD
Other Current Liab—11,134,000USD11,394,000USD9,424,000USD9,097,000USD6,849,000USD10,822,000USD10,438,000USD
Capital Stock—0USD0USD0USD0USD0USD0USD0USD
Cash—124,161,000USD103,845,000USD71,005,000USD58,813,000USD70,771,000USD136,586,000USD66,633,000USD
Net Debt—-115,031,000USD-93,954,000USD-59,732,000USD-45,960,000USD-57,228,000USD-124,158,000USD-52,100,000USD
Short Long Term Debt Total—9,130,000USD9,891,000USD11,273,000USD12,853,000USD13,543,000USD12,428,000USD14,533,000USD
Property Plant Equipment Gross—29,933,000USD29,571,000USD29,340,000USD29,561,000USD29,587,000USD29,664,000USD29,732,000USD
Common Stock Shares Outstanding—22,305,734shares15,489,800shares21,168,431shares21,055,378shares20,996,287shares14,854,725shares16,953,443shares
Non Current Assets Total—16,394,000USD17,596,999USD17,313,000USD18,330,000USD18,903,000USD19,807,000USD20,473,000USD
Non Current Liabilities Total—6,492,000USD7,878,000USD7,582,000USD8,621,000USD9,412,000USD10,198,000USD10,906,000USD
Non Currrent Assets Other—1,417,000USD1,223,999USD1,402,000USD1,435,000USD1,235,000USD1,314,000USD1,128,000USD
Net Working Capital—227,881,000USD255,359,000USD255,809,000USD263,546,000USD282,304,000USD300,766,000USD127,847,000USD
Unclassified Non Current Liabilities—6,492,000USD7,827,000USD7,531,000USD8,570,000USD9,361,000USD10,147,000USD10,855,000USD
Unclassified Equity—621,366,000USD617,536,000USD593,454,000USD580,216,000USD576,740,000USD572,673,000USD380,198,000USD
Net Receivables——460,000USD860,000USD1,309,000USD596,000USD648,000USD672,000USD
Non Current Liabilities Other——51,000USD51,000USD51,000USD51,000USD51,000USD51,000USD
Other Assets——————-714,000USD—
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Balance sheet Yearly

Exact reported values; units shown beside each amount. Missing values are —.
MetricFY 20252025-12-31 · USDFY 20242024-12-31 · USDFY 20232023-12-31 · USDFY 20222022-12-31 · USDFY 20212021-12-31 · USDFY 20202020-12-31 · USDFY 20192019-12-31 · USDFY 20182018-12-31 · USD
Total Assets288,604,000USD335,730,000USD222,573,000USD109,265,000USD101,487,000USD210,519,000USD147,023,000USD77,618,000USD
Other Current Assets2,757,000USD2,870,000USD2,591,000USD2,698,000USD711,000USD1,966,000USD503,000USD237,000USD
Total Liab23,717,000USD25,355,000USD36,549,000USD10,638,000USD193,362,000USD19,303,000USD5,336,000USD4,946,000USD
Total Stockholder Equity264,887,000USD310,375,000USD186,024,000USD98,627,000USD-91,875,000USD191,216,000USD141,687,000USD72,672,000USD
Other Current Liab11,394,000USD10,822,000USD17,495,000USD5,324,000USD3,395,000USD5,858,000USD2,521,000USD3,925,000USD
Capital Stock0USD0USD0USD1,000USD1,000USD———
Retained Earnings-352,649,000USD-262,298,000USD-187,154,000USD-150,837,000USD-95,648,000USD-332,806,000USD-299,529,000USD-230,087,000USD
Cash103,845,000USD136,586,000USD148,210,000USD82,021,000USD70,544,000USD192,556,000USD143,093,000USD76,928,000USD
Cash And Short Term Investments269,013,000USD312,405,000USD197,157,000USD82,021,000USD70,544,000USD192,556,000USD143,093,000USD76,928,000USD
Total Current Assets271,770,000USD315,923,000USD200,348,000USD84,719,000USD73,958,000USD194,522,000USD143,596,000USD77,165,000USD
Total Current Liabilities16,411,000USD15,157,000USD22,973,000USD6,651,000USD10,856,000USD7,889,000USD4,743,000USD4,627,000USD
Net Debt-93,954,000USD-124,158,000USD-131,955,000USD-77,332,000USD-64,114,000USD-180,434,000USD-141,882,000USD-76,922,000USD
Short Term Debt3,064,000USD2,999,000USD2,882,000USD702,000USD1,831,000USD708,000USD618,000USD—
Short Long Term Debt Total9,891,000USD12,428,000USD16,255,000USD4,689,000USD6,430,000USD12,122,000USD1,211,000USD6,000USD
Short Term Investments165,168,000USD175,819,000USD48,947,000USD58,497,000USD————
Accounts Payable1,953,000USD1,336,000USD2,596,000USD625,000USD5,630,000USD1,323,000USD1,604,000USD702,000USD
Property Plant Equipment Net15,462,000USD18,493,000USD20,953,000USD24,546,000USD27,529,000USD13,724,000USD2,830,000USD400,000USD
Property Plant Equipment Gross29,571,000USD29,664,000USD28,864,000USD29,226,000USD29,100,000USD———
Common Stock Shares Outstanding21,168,431shares17,567,082shares12,823,665shares12,823,665shares55,041,662shares51,825,022shares27,030,355shares23,519,508shares
Non Current Assets Total16,834,000USD19,807,000USD22,225,000USD24,546,000USD27,529,000USD15,997,000USD3,427,000USD453,000USD
Non Current Liabilities Total7,306,000USD10,198,000USD13,576,000USD3,987,000USD182,506,000USD11,414,000USD593,000USD319,000USD
Non Current Liabilities Other51,000USD51,000USD203,000USD—————
Non Currrent Assets Other1,372,000USD1,314,000USD1,272,000USD-791,000USD-1,006,000USD1,926,000USD30,000USD52,999USD
Net Working Capital255,359,000USD300,766,000USD177,375,000USD78,068,000USD63,102,000USD———
Unclassified Non Current Liabilities7,255,000USD10,147,000USD13,373,000USD3,987,000USD182,506,000USD11,414,000USD——
Unclassified Equity617,536,000USD572,673,000USD373,178,000USD249,462,000USD3,771,000USD524,022,000USD441,216,000USD302,759,000USD
Net Receivables—648,000USD600,000USD990,000USD790,000USD———
Current Deferred Revenue——16,758,000USD5,157,000USD4,349,000USD———
Inventory——1,496,000USD1,078,000USD1,913,000USD———
Unclassified Current Liabilities——-16,758,000USD-5,157,000USD-4,349,000USD———
Common Stock———1,000USD1,000USD———
Accumulated Other Comprehensive Income———0USD0USD———
Unclassified Current Assets———-60,565,000USD————
Intangible Assets————128,000USD347,000USD567,000USD—
Other Assets——————1USD1USD
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Cash flow YTD

Exact reported values; units shown beside each amount. Missing values are —.
MetricQ2 20262026-06-30 · USD
Depreciation1,660,000USD
Stock Based Compensation11,491,000USD
Change To Liabilities5,752,000USD
Change In Working Capital450,000USD
Operating Cash Flow-49,880,000USD
Capital Expenditures-635,000USD
Unclassified Investing Cash Flow52,979,000USD
Investing Cash Flow52,344,000USD
Net Debt Issuance-11,000USD
Unclassified Financing Cash Flow6,187,000USD
Financing Cash Flow6,176,000USD
Change In Cash8,640,000USD
End Cash Flow112,824,000USD
SourceDisclosureDeterministicFinal

Cash flow Quarterly

Exact reported values; units shown beside each amount. Missing values are —.
MetricQ1 20262026-03-31 · USDQ4 20252025-12-31 · USDQ3 20252025-09-30 · USDQ2 20252025-06-30 · USDQ1 20252025-03-31 · USDQ4 20242024-12-31 · USDQ3 20242024-09-30 · USDQ2 20242024-06-30 · USD
Net Income-30,934,000USD-24,735,000USD-20,953,000USD-22,016,000USD-22,647,000USD-19,514,000USD-20,217,000USD-18,492,000USD
Depreciation854,000USD787,000USD812,000USD767,000USD762,000USD798,000USD807,000USD817,000USD
Stock Based Compensation3,629,000USD3,362,000USD3,365,000USD3,408,000USD4,048,000USD2,487,000USD2,474,000USD2,314,000USD
Other Non Cash Items2,788,000USD3,878,454USD1,737,143USD-1,220,000USD-1,523,000USD-371,000USD-1,191,000USD580,000USD
Change In Working Capital1,173,000USD3,395,865USD-1,278,734USD-401,000USD-1,414,000USD-896,000USD2,563,000USD-1,112,000USD
Total Cash From Operating Activities-26,119,000USD-16,673,681USD-19,682,590USD-19,462,000USD-20,774,000USD-17,496,000USD-15,564,000USD-15,893,000USD
Capital Expenditures-281,000USD-114,289USD-126,109USD-148,000USD-780,000USD-116,000USD-167,000USD-460,000USD
Free Cash Flow-26,400,000USD-16,787,970USD-19,808,700USD-19,610,000USD-21,554,000USD-17,612,000USD-15,731,000USD-16,353,000USD
Investments46,521,000USD29,737,000USD21,990,000USD7,450,000USD-45,045,000USD-102,616,000USD-28,966,000USD-23,614,000USD
Total Cashflows From Investing Activities46,240,000USD29,878,093USD22,438,846USD7,450,000USD-45,045,000USD-102,616,000USD-28,966,000USD-23,614,000USD
Net Borrowings-6,000USD-19,000USD-13,000USD-14,000USD-15,000USD-13,000USD-12,000USD—
Total Cash From Financing Activities195,000USD20,573,943USD9,857,577USD54,000USD4,000USD190,065,000USD131,000USD399,000USD
Change In Cash20,316,000USD32,840,000USD12,192,000USD-11,958,000USD-65,815,000USD69,953,000USD-44,399,000USD-39,108,000USD
Begin Period Cash Flow103,845,000USD71,005,000USD58,813,000USD71,110,000USD136,925,000USD66,972,000USD111,371,000USD150,140,000USD
End Period Cash Flow124,161,000USD103,845,000USD71,005,000USD59,152,000USD71,110,000USD136,925,000USD66,972,000USD111,032,000USD
Other Cashflows From Investing Activities130,000,000USD—99,500,000USD68,000,000USD44,700,000USD—-20,854,000USD-42,303,700USD
Other Cashflows From Financing Activities195,000USD—9,710,000USD-1,588USD19,000USD3,890,994USD-2,763USD7,389USD
Unclassified Operating Cash Flow-3,629,000USD-3,362,000USD-3,364,999USD—————
Unclassified Investing Cash Flow-130,000,000USD—-98,925,045USD-67,852,000USD-43,920,000USD—21,021,000USD42,763,700USD
Issuance Of Capital Stock—20,580,000USD——————
Unclassified Financing Cash Flow—————186,187,006USD——
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Cash flow Yearly

Exact reported values; units shown beside each amount. Missing values are —.
MetricFY 20252025-12-31 · USDFY 20242024-12-31 · USDFY 20232023-12-31 · USDFY 20222022-12-31 · USDFY 20212021-12-31 · USDFY 20202020-12-31 · USDFY 20192019-12-31 · USDFY 20182018-12-31 · USD
Net Income-90,351,000USD-75,144,000USD-36,317,000USD-55,189,000USD-50,517,000USD-33,277,000USD-8,101,000USD-31,585,000USD
Depreciation3,092,000USD3,247,000USD3,297,000USD3,200,000USD947,000USD1,821,000USD340,000USD—
Stock Based Compensation14,183,000USD8,320,000USD1,418,000USD1,252,000USD896,000USD———
Other Non Cash Items-4,365,000USD-1,065,000USD-15,692,000USD608,000USD679,000USD5,915,000USD-5,679,000USD5,439,000USD
Change In Working Capital268,000USD-5,961,000USD-4,023,000USD-2,695,000USD1,595,000USD966,000USD-1,954,000USD-5,431,000USD
Total Cash From Operating Activities-77,173,000USD-70,603,000USD-51,422,000USD-52,824,000USD-46,400,000USD-24,575,000USD-15,394,000USD-31,577,000USD
Capital Expenditures-1,183,000USD-808,000USD-321,000USD-2,230,000USD-18,369,000USD-2,219,000USD-879,000USD-49,000USD
Free Cash Flow-78,356,000USD-71,411,000USD-51,743,000USD-55,054,000USD-64,769,000USD-26,794,000USD-16,273,000USD-31,626,000USD
Investments15,187,000USD-125,261,000USD25,637,000USD-2,230,000USD-18,369,000USD———
Total Cashflows From Investing Activities14,004,000USD-125,261,000USD25,637,000USD-2,230,000USD-18,369,000USD-2,219,000USD-688,000USD55,951,000USD
Net Borrowings-61,000USD-52,000USD-29,000USD-1,000USD0USD———
Total Cash From Financing Activities30,428,000USD184,071,000USD92,482,000USD66,531,000USD51,063,000USD77,135,000USD82,237,000USD570,000USD
Issuance Of Capital Stock30,380,000USD189,589,000USD92,343,000USD66,459,000USD50,776,000USD———
Change In Cash-32,741,000USD-11,793,000USD66,697,000USD11,477,000USD-13,706,000USD49,463,000USD66,165,000USD24,896,000USD
Begin Period Cash Flow136,925,000USD148,718,000USD82,021,000USD70,544,000USD84,250,000USD143,093,000USD76,928,000USD52,032,000USD
End Period Cash Flow104,184,000USD136,925,000USD148,718,000USD82,021,000USD70,544,000USD192,556,000USD143,093,000USD76,928,000USD
Other Cashflows From Investing Activities—74,000,000USD20,958,000USD—————
Other Cashflows From Financing Activities—-5,466,000USD168,000USD66,532,000USD51,063,000USD-2,219,000USD-688,000USD55,951,000USD
Unclassified Investing Cash Flow—-73,192,000USD-20,637,000USD2,230,000USD18,369,000USD——56,000,000USD
Unclassified Financing Cash Flow———-66,459,000USD-50,776,000USD79,354,000USD82,925,000USD-55,381,000USD
Change To Account Receivables——————290,000USD—
SourceLegacy providerLegacyLegacy providerLegacyLegacy providerLegacyLegacy providerLegacyLegacy providerLegacyLegacy providerLegacyLegacy providerLegacyLegacy providerLegacy

Operating metrics

No operating metrics are currently published for this company.

Revenue breakdown

No revenue breakdown is currently published for this company.

Periods follow company fiscal calendars. Quarterly, annual and year-to-date amounts are shown separately. Missing values are not zero. Data may be delayed, incomplete or corrected; follow the disclosure links to verify figures.