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DSGN

Design Therapeutics, Inc.

Company overview

Market capitalization
$773.51M
Employees
54
Latest publication
2026-09-29
About Design Therapeutics, Inc.

Design Therapeutics, Inc. a clinical-stage biopharmaceutical company, research, designs, develops, and commercializes small molecule therapeutic drugs for the treatment of genetic diseases in the United States. The company utilizes its GeneTAC platform to design and develop therapeutic candidates for inherited diseases caused by nucleotide repeat expansion. Its lead product candidates for potentially disease-modifying treatment comprises Friedreich Ataxia, a monogenic, autosomal recessive, progressive multi-system disease that affects organ systems dependent on mitochondrial function that brings to neurological, cardiac, and metabolic dysfunction; Myotonic Dystrophy Type-1, a dominantly-inherited, monogenic progressive neuromuscular disease affecting skeletal muscle, heart, brain, and other organs; Fuchs Endothelial Corneal Dystrophy, a genetic eye disease characterized by bilateral degeneration of corneal endothelial cells and progressive loss of vision; and Huntington's Disease, a dominantly inherited, monogenic neurodegenerative disease characterized by movement, cognitive, and psychiatric disorders. The company was incorporated in 2017 and is headquartered in Carlsbad, California.

Company website

Financial statements

Income Quarterly

Exact reported values; units shown beside each amount. Missing values are —.
MetricQ1 20262026-03-31 · USDQ4 20252025-12-31 · USDQ3 20252025-09-30 · USDQ2 20252025-06-30 · USDQ1 20252025-03-31 · USDQ4 20242024-12-31 · USDQ3 20242024-09-30 · USDQ2 20242024-06-30 · USD
Total Revenue0USD0USD0USD0USD0USD588,000USD0USD0USD
Research Development14,379,000USD13,425,000USD14,589,000USD15,738,000USD15,377,000USD12,157,000USD11,876,000USD10,365,000USD
Selling General Administrative5,327,000USD4,814,000USD4,652,000USD5,831,000USD5,041,000USD4,537,000USD4,370,000USD4,451,000USD
Total Operating Expenses19,706,000USD32,910,000USD4,722,000USD21,417,000USD20,418,000USD16,694,000USD16,246,000USD14,892,000USD
Operating Income-19,706,000USD-18,169,000USD-19,311,000USD-21,569,000USD-20,418,000USD-16,694,000USD-16,246,000USD-15,043,000USD
Interest Income2,070,000USD2,172,000USD2,314,000USD2,486,000USD2,703,000USD——3,250,000USD
Net Interest Income2,070,000USD2,172,000USD2,314,000USD2,486,000USD2,703,000USD——3,250,000USD
Income Before Tax-17,636,000USD-15,997,000USD-16,997,000USD-19,083,000USD-17,715,000USD-13,651,000USD-13,039,000USD-11,793,000USD
Net Income-17,636,000USD-15,997,000USD-16,997,000USD-19,083,000USD-17,715,000USD-13,651,000USD-13,039,000USD-11,793,000USD
Net Income From Continuing Ops-17,636,000USD-15,997,000USD-16,997,000USD-19,083,000USD-17,715,000USD-13,651,000USD-13,039,000USD-11,793,000USD
Ebit-17,636,000USD-15,997,000USD-16,997,000USD-19,083,000USD-17,715,000USD-13,651,000USD-13,039,000USD-11,793,000USD
Ebitda-17,479,000USD-15,841,000USD-16,842,000USD-18,931,000USD-17,556,000USD-13,502,000USD-12,886,000USD-11,642,000USD
Depreciation And Amortization157,000USD156,000USD155,000USD152,000USD159,000USD149,000USD153,000USD151,000USD
Reconciled Depreciation157,000USD156,000USD155,000USD152,000USD159,000USD149,000USD153,000USD151,000USD
Total Other Income Expense Net2,070,000USD2,172,000USD2,314,000USD2,486,000USD2,703,000USD3,043,000USD3,207,000USD3,250,000USD
Cost Of Revenue—-14,741,000USD14,589,000USD152,000USD159,000USD149,000USD153,000USD151,000USD
Gross Profit—14,741,000USD-14,589,000USD-152,000USD-159,000USD294,000USD-153,000USD-151,000USD
Selling And Marketing Expenses—70,000USD—————76,000USD
Unclassified Operating Expenses—14,601,000USD-14,519,000USD—————
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Income Yearly

Exact reported values; units shown beside each amount. Missing values are —.
MetricFY 20252025-12-31 · USDFY 20242024-12-31 · USDFY 20232023-12-31 · USDFY 20222022-12-31 · USDFY 20212021-12-31 · USDFY 20202020-12-31 · USDFY 20192019-12-31 · USD
Total Revenue0USD0USD0USD0USD0USD226USD834,000USD
Cost Of Revenue622,000USD596,000USD537,000USD466,000USD129,000USD5,000USD1,654USD
Gross Profit-622,000USD-596,000USD-537,000USD-466,000USD-129,000USD-5,000USD-820USD
Research Development59,129,000USD44,350,000USD57,063,000USD48,613,000USD24,778,000USD6,060,000USD1,654,000USD
Selling General Administrative20,338,000USD18,033,000USD21,127,000USD18,980,000USD11,053,000USD2,496,000USD1,088,000USD
Total Operating Expenses78,845,000USD61,787,000USD77,653,000USD67,593,000USD35,831,000USD8,551,000USD1,908,000USD
Operating Income-79,467,000USD-62,383,000USD-78,190,000USD-67,593,000USD-35,831,000USD-8,556,000USD-1,908,000USD
Interest Income9,675,000USD12,795,000USD11,328,000USD————
Net Interest Income9,675,000USD12,795,000USD11,328,000USD————
Income Before Tax-69,792,000USD-49,588,000USD-66,862,000USD-63,308,000USD-35,533,000USD-8,280,000USD-2,047,000USD
Net Income-69,792,000USD-49,588,000USD-66,862,000USD-58,617,000USD-35,533,000USD-8,280,000USD-2,047,000USD
Net Income From Continuing Ops-69,792,000USD-49,588,000USD-72,360,000USD-63,308,000USD-35,533,000USD-8,280,000USD-2,047,000USD
Ebit-69,792,000USD-49,588,000USD-66,862,000USD-67,593,000USD-35,533,000USD-8,280,000USD-1,908,000USD
Ebitda-69,170,000USD-48,992,000USD-66,325,000USD-67,187,000USD-35,404,000USD-8,275,000USD-1,908,000USD
Depreciation And Amortization622,000USD596,000USD537,000USD406,000USD129,000USD5,000USD1,908USD
Reconciled Depreciation622,000USD596,000USD523,000USD406,000USD129,000USD5,000USD0USD
Total Other Income Expense Net9,675,000USD12,795,000USD11,328,000USD4,285,000USD298,000USD276,000USD-139,000USD
Income Tax Expense——-1USD-4,691,000USD-107,558USD-201,297USD139,000USD
Interest Expense———4,691,000USD298,000USD0USD0USD
Non Operating Income Net Other———4,285,000USD298,000USD——
Net Income Applicable To Common Shares———-63,308,000USD-35,533,000USD-8,280,000USD-2,047,000USD
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Balance sheet Quarterly

Exact reported values; units shown beside each amount. Missing values are —.
MetricQ2 20262026-06-30 · USDQ1 20262026-03-31 · USDQ4 20252025-12-31 · USDQ3 20252025-09-30 · USDQ2 20252025-06-30 · USDQ1 20252025-03-31 · USDQ4 20242024-12-31 · USDQ3 20242024-09-30 · USD
Total Assets215,129,000USD230,442,000USD226,203,000USD211,770,000USD222,886,000USD237,475,000USD252,093,000USD261,629,000USD
Cash And Equivalents12,907,000USD———————
Cash And Short Term Investments207,396,000USD222,823,000USD219,845,000USD205,970,000USD216,276,000USD229,674,000USD245,477,000USD254,074,000USD
Short Term Investments194,489,000USD210,053,000USD202,989,000USD190,882,000USD196,573,000USD216,007,000USD222,914,000USD223,746,000USD
Total Current Assets212,013,000USD227,049,000USD223,784,000USD209,029,000USD219,794,000USD233,644,000USD248,040,000USD257,242,000USD
Other Current Assets4,617,000USD2,403,000USD2,262,000USD1,678,000USD2,170,000USD2,565,000USD1,300,000USD1,989,000USD
Total Liabilities13,271,000USD———————
Total Current Liabilities11,240,000USD10,190,000USD13,055,000USD11,173,000USD8,747,000USD8,236,000USD8,462,000USD7,432,000USD
Total Stockholder Equity201,858,000USD218,054,000USD212,503,000USD199,720,000USD213,037,000USD227,919,000USD242,097,000USD252,453,000USD
Total Equity Including Noncontrolling Interest201,858,000USD———————
Property Plant Equipment Net3,116,000USD3,393,000USD2,419,000USD2,741,000USD3,092,000USD3,404,000USD3,626,000USD3,960,000USD
Accounts Payable3,141,000USD2,276,000USD2,312,000USD1,913,000USD1,013,000USD3,180,000USD2,186,000USD1,470,000USD
Common Stock6,000USD6,000USD6,000USD6,000USD6,000USD6,000USD6,000USD6,000USD
Retained Earnings-334,807,000USD-314,642,000USD-297,006,000USD-281,009,000USD-264,012,000USD-244,929,000USD-227,214,000USD-213,563,000USD
Accumulated Other Comprehensive Income-771,000USD-268,000USD403,000USD358,000USD305,000USD450,000USD475,000USD914,000USD
Total Liab—12,388,000USD13,700,000USD12,050,000USD9,849,000USD9,556,000USD9,996,000USD9,176,000USD
Other Current Liab—7,378,000USD9,853,000USD8,394,000USD6,890,000USD4,235,000USD5,476,000USD5,184,000USD
Capital Stock—6,000USD6,000USD6,000USD6,000USD6,000USD6,000USD6,000USD
Cash—12,770,000USD16,856,000USD15,088,000USD19,703,000USD13,667,000USD22,563,000USD30,328,000USD
Net Debt—-10,036,000USD-15,321,000USD-13,345,000USD-17,757,000USD-11,526,000USD-20,229,000USD-27,806,000USD
Short Term Debt—536,000USD890,000USD866,000USD844,000USD821,000USD800,000USD778,000USD
Short Long Term Debt Total—2,734,000USD1,535,000USD1,743,000USD1,946,000USD2,141,000USD2,334,000USD2,522,000USD
Net Receivables—1,823,000USD1,677,000USD1,381,000USD1,348,000USD1,405,000USD1,263,000USD1,179,000USD
Property Plant Equipment Gross—5,814,000USD4,683,000USD4,849,000USD5,047,000USD5,207,000USD5,281,000USD5,466,000USD
Common Stock Shares Outstanding—61,434,457shares57,330,192shares56,950,999shares56,859,388shares56,757,827shares56,681,940shares56,620,731shares
Non Current Assets Total—3,393,000USD2,419,000USD2,741,000USD3,092,000USD3,831,000USD4,053,000USD4,387,000USD
Non Current Liabilities Total—2,198,000USD645,000USD877,000USD1,102,000USD1,320,000USD1,534,000USD1,744,000USD
Net Working Capital—216,859,000USD210,729,000USD197,856,000USD211,047,000USD225,408,000USD239,578,000USD249,810,000USD
Unclassified Non Current Liabilities—2,198,000USD——1,102,000USD1,320,000USD1,534,000USD1,744,000USD
Unclassified Equity—532,952,000USD509,094,000USD480,359,000USD476,732,000USD472,386,000USD468,824,000USD465,090,000USD
Non Currrent Assets Other—————427,000USD427,000USD427,000USD
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Balance sheet Yearly

Exact reported values; units shown beside each amount. Missing values are —.
MetricFY 20252025-12-31 · USDFY 20242024-12-31 · USDFY 20232023-12-31 · USDFY 20222022-12-31 · USDFY 20212021-12-31 · USDFY 20202020-12-31 · USDFY 20192019-12-31 · USD
Total Assets226,203,000USD252,093,000USD289,643,000USD341,137,000USD390,557,000USD36,516,000USD90,000USD
Other Current Assets2,262,000USD1,300,000USD1,354,000USD3,617,000USD1,261,000USD132,000USD13,000USD
Total Liab13,700,000USD9,996,000USD11,956,000USD13,827,000USD8,427,000USD47,831,000USD3,732,000USD
Total Stockholder Equity212,503,000USD242,097,000USD277,687,000USD327,310,000USD382,130,000USD-11,315,000USD-3,642,000USD
Other Current Liab9,853,000USD5,476,000USD6,966,000USD7,111,000USD3,174,000USD931,000USD356,000USD
Common Stock6,000USD6,000USD6,000USD6,000USD6,000USD1,000USD1,000USD
Capital Stock6,000USD6,000USD6,000USD6,000USD6,000USD1,000USD1,000USD
Retained Earnings-297,006,000USD-227,214,000USD-177,626,000USD-110,764,000USD-47,456,000USD-11,923,000USD-3,643,000USD
Cash16,856,000USD22,563,000USD21,200,000USD26,500,000USD298,569,000USD2,379,000USD77,000USD
Cash And Short Term Investments219,845,000USD245,477,000USD281,798,000USD330,387,000USD384,064,000USD36,091,000USD77,000USD
Total Current Assets223,784,000USD248,040,000USD284,584,000USD335,119,000USD385,435,000USD36,233,000USD90,000USD
Total Current Liabilities13,055,000USD8,462,000USD9,622,000USD10,776,000USD5,283,000USD2,330,000USD3,731,000USD
Net Debt-15,321,000USD-20,229,000USD-18,150,000USD-22,809,000USD-294,936,000USD-2,379,000USD618,000USD
Short Term Debt890,000USD800,000USD716,000USD640,000USD489,000USD—695,000USD
Short Long Term Debt Total1,535,000USD2,334,000USD3,050,000USD3,691,000USD3,633,000USD—695,000USD
Short Term Investments202,989,000USD222,914,000USD260,598,000USD303,887,000USD85,495,000USD33,712,000USD0USD
Net Receivables1,677,000USD1,263,000USD1,432,000USD1,115,000USD110,000USD10,000USD—
Accounts Payable2,312,000USD2,186,000USD1,940,000USD3,025,000USD1,620,000USD1,399,000USD2,479,000USD
Property Plant Equipment Net2,419,000USD3,626,000USD4,629,000USD5,559,000USD5,122,000USD71,000USD0USD
Property Plant Equipment Gross4,683,000USD5,281,000USD5,688,000USD5,559,000USD5,256,000USD71,000USD0USD
Accumulated Other Comprehensive Income403,000USD475,000USD62,000USD-3,356,000USD-244,000USD156,000USD—
Common Stock Shares Outstanding57,330,192shares56,587,142shares55,984,670shares55,707,517shares45,940,000shares27,190,000shares27,190,000shares
Non Current Assets Total2,419,000USD4,053,000USD5,059,000USD6,018,000USD5,122,000USD283,000USD0USD
Non Current Liabilities Total645,000USD1,534,000USD2,334,000USD3,051,000USD3,144,000USD45,501,000USD1,000USD
Net Working Capital210,729,000USD239,578,000USD274,962,000USD324,343,000USD380,152,000USD33,903,000USD-3,641,000USD
Unclassified Equity509,094,000USD468,824,000USD455,239,000USD441,418,000USD429,818,000USD——
Non Currrent Assets Other—427,000USD430,000USD459,000USD-85,495USD212,000USD—
Unclassified Non Current Liabilities—1,534,000USD2,334,000USD——44,999,000USD—
Other Assets——1USD459,000USD—212,000USD—
Inventory———-1,115,000USD1,254,000USD107,000USD—
Non Current Liabilities Other———3,051,000USD3,144,000USD145,000USD1,000USD
Net Tangible Assets———327,310,000USD382,130,000USD-11,315,000USD-3,642,000USD
Deferred Long Term Liab—————212,000USD—
Other Liab—————145,000USD1,000USD
Current Deferred Revenue——————201,000USD
Short Long Term Debt——————695,000USD
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Cash flow Quarterly

Exact reported values; units shown beside each amount. Missing values are —.
MetricQ1 20262026-03-31 · USDQ4 20252025-12-31 · USDQ3 20252025-09-30 · USDQ2 20252025-06-30 · USDQ1 20252025-03-31 · USDQ4 20242024-12-31 · USDQ3 20242024-09-30 · USDQ2 20242024-06-30 · USD
Net Income-17,636,000USD-15,997,000USD-16,997,000USD-19,083,000USD-17,715,000USD-13,651,000USD-13,039,000USD-11,793,000USD
Depreciation10,000USD704,000USD155,000USD152,000USD159,000USD149,000USD153,000USD151,000USD
Stock Based Compensation3,924,000USD3,435,000USD3,590,000USD3,985,000USD3,539,000USD3,471,000USD3,118,000USD3,299,000USD
Other Non Cash Items69,000USD-1,068,000USD-774,000USD-489,000USD-1,064,000USD-1,441,000USD-1,455,000USD-1,569,000USD
Change In Working Capital-2,798,000USD960,000USD2,864,000USD994,000USD-1,708,000USD1,612,000USD1,677,000USD-1,348,000USD
Total Cash From Operating Activities-16,431,000USD-11,966,000USD-11,162,000USD-14,441,000USD-16,789,000USD-9,860,000USD-9,546,000USD-11,260,000USD
Capital Expenditures0USD-34,000USD0USD-87,000USD-72,000USD0USD-16,000USD-161,000USD
Free Cash Flow-16,431,000USD-12,000,000USD-11,162,000USD-14,528,000USD-16,861,000USD-9,860,000USD-9,530,000USD-11,421,000USD
Investments-7,589,000USD-11,549,000USD6,510,000USD20,116,000USD7,870,000USD1,832,000USD-5,826,000USD27,333,000USD
Total Cashflows From Investing Activities-7,589,000USD-11,583,000USD6,510,000USD20,116,000USD7,870,000USD1,832,000USD-5,826,000USD27,333,000USD
Total Cash From Financing Activities19,934,000USD25,317,000USD37,000USD361,000USD23,000USD263,000USD1,000USD229,000USD
Issuance Of Capital Stock19,907,000USD———0USD———
Change In Cash-4,086,000USD1,768,000USD-4,615,000USD6,036,000USD-8,896,000USD-7,765,000USD-15,371,000USD16,302,000USD
Begin Period Cash Flow16,856,000USD15,088,000USD19,703,000USD13,667,000USD22,563,000USD30,328,000USD45,699,000USD29,397,000USD
End Period Cash Flow12,770,000USD16,856,000USD15,088,000USD19,703,000USD13,667,000USD22,563,000USD30,328,000USD45,699,000USD
Other Cashflows From Financing Activities19,934,000USD25,317,000USD37,000USD—23,000USD263,000USD1,000USD229,000USD
Unclassified Financing Cash Flow-19,907,000USD———————
Sale Purchase Of Stock—288,000USD—361,000USD——223,000USD—
Other Cashflows From Investing Activities———————27,494USD
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Cash flow Yearly

Exact reported values; units shown beside each amount. Missing values are —.
MetricFY 20252025-12-31 · USDFY 20242024-12-31 · USDFY 20232023-12-31 · USDFY 20212021-12-31 · USDFY 20202020-12-31 · USDFY 20192019-12-31 · USD
Net Income-69,792,000USD-49,588,000USD-66,862,000USD-35,533,000USD-8,280,000USD-2,047,000USD
Depreciation-2,631,000USD596,000USD537,000USD129,000USD5,000USD5,000USD
Stock Based Compensation14,549,000USD13,072,000USD13,088,000USD4,689,000USD450,000USD0USD
Other Non Cash Items406,000USD-6,192,000USD-6,051,000USD-58,000USD-33,000USD95,000USD
Change In Working Capital3,110,000USD-993,000USD728,000USD1,396,000USD-811,000USD1,813,000USD
Total Cash From Operating Activities-54,358,000USD-43,105,000USD-58,560,000USD-29,377,000USD-8,669,000USD-139,000USD
Capital Expenditures-193,000USD-340,000USD-256,000USD-1,538,000USD-76,000USD-76,000USD
Free Cash Flow-54,551,000USD-43,445,000USD-58,816,000USD-30,915,000USD-8,745,000USD-139,000USD
Investments23,106,000USD43,955,000USD45,925,000USD-52,106,000USD-33,485,000USD-33,485,000USD
Total Cashflows From Investing Activities22,913,000USD43,955,000USD52,536,000USD-53,644,000USD-33,561,000USD-33,561,000USD
Total Cash From Financing Activities25,738,000USD513,000USD724,000USD379,211,000USD44,532,000USD196,000USD
Sale Purchase Of Stock649,000USD477,000USD305,000USD194,000USD——
Issuance Of Capital Stock24,847,000USD0USD—378,983,000USD44,731,000USD0USD
Change In Cash-5,707,000USD1,363,000USD-5,300,000USD296,190,000USD2,302,000USD57,000USD
Begin Period Cash Flow22,563,000USD21,200,000USD26,500,000USD2,379,000USD77,000USD20,000USD
End Period Cash Flow16,856,000USD22,563,000USD21,200,000USD298,569,000USD2,379,000USD77,000USD
Other Cashflows From Financing Activities25,738,000USD513,000USD724,000USD124,940,000USD44,732,000USD396,000USD
Unclassified Investing Cash Flow——6,867,000USD———
Change To Liabilities———2,418,000USD-614,000USD1,823,000USD
Net Borrowings———0USD-200,000USD196,000USD
Cash And Cash Equivalents Changes———296,190,000USD——
Other Cashflows From Investing Activities———-52,106USD-33,485USD—
Unclassified Financing Cash Flow———254,077,000USD-44,731,000USD—
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Operating metrics

No operating metrics are currently published for this company.

Revenue breakdown

No revenue breakdown is currently published for this company.

Periods follow company fiscal calendars. Quarterly, annual and year-to-date amounts are shown separately. Missing values are not zero. Data may be delayed, incomplete or corrected; follow the disclosure links to verify figures.